Planned CHOICES Trial in Rare CF Mutations Given Regulatory Support
Proteostasis Therapeutics reported receiving scientific advice for its CHOICES clinical trial program, which is to test its personalized...
Simulations show how to make gene therapy more effective
Visualisation of a lipoplex entrapped inside an endosome. The DNA (yellow/pink rods) can only escape upon fusion of the lipoplex (red)...
Breaking the Diagnosis of Cystic Fibrosis to Parents: A process not a one-off event
2019 Royal Society of Medicine Cystic Fibrosis Symposium Breaking the Diagnosis of Cystic Fibrosis to Parents: A process not a one-off...
Coronavirus update: More considered vulnerable - full list of who should stay at home
CORONAVIRUS can be dangerous for the most vulnerable members of society. As time goes on, more health conditions - that increase a...
Arrowhead Pharmaceuticals files for regulatory clearance to begin phase 1/2a study of ARO-ENaC for t
rrowhead Pharmaceuticals has filed an application for clearance to begin a Phase 1/2a clinical trial of ARO-ENaC, the company’s...
McGill spinoff Laurent Pharmaceuticals to begin clinical trial on COVID-19 treatment
Company to run a Phase 2 clinical study with LAU-7b, a pro-resolving drug with potential antiviral properties against coronavirus Junji...
Verona Pharma Reports Positive Efficacy and Safety Data with Single Dose pMDI Formulation of Ensifen
Statistically significant and clinically meaningful improvements in lung function Ensifentrine has now demonstrated positive efficacy and...
UHG Adult Cystic Fibrosis Team to use online videos for outpatient consultations
Galway Bay fm newsroom: The Adult Cystic Fibrosis Team at UHG will use online video conferencing instead of face-to-face outpatient...
CF Patients’ Risk For Ototoxicity Underreported
Las Vegas—The complex needs of patients with cystic fibrosis (CF) who are managed by specialty pharmacies just got a bit more complicated...
Study Finds Funding Disparities Between Sickle Cell Disease, Cystic Fibrosis
Disparities in funding exist between sickle cell disease (SCD) and cystic fibrosis (CF), according to a new study published in JAMA...
