Ultrasound Can Help Detect Liver Disease in Kids with CF, Study Says
Ultrasound imaging can be a reliable diagnostic tool for early detection of liver disease in children with cystic fibrosis (CF), a study...


BillionToOne Announces Launch of UNITY Prenatal Screen
The diagnostics company BillionToOne has launched its first product for commercial and clinical use — a blood test designed to help...


FDA Grants Orphan Drug Status to AR-501, Potential CF Treatment for Chronic Lung Infections
AR-501, an investigational inhaled formulation of gallium citrate to treat chronic lung infections in patients with cystic fibrosis (CF),...


‘Rare Barometer’ Program Helps Eurordis Shape EU Rare Disease Policy
People with rare diseases know that the right government policies can make a big difference in the quality of their own lives, and those...


EffRx Pharmaceuticals Signs Exclusive License Agreement with Pharmaxis for the Registration and Comm
EffRx Pharmaceuticals SA, a commercial-stage company that commercializes niche and orphan medicines in Switzerland and Europe, today...
New study confirms vaping is not safer than smoking- it obstructs mucus clearance
Research published in the American Thoracic Society’s American Journal of Respiratory and Critical Care Medicine confirms that...


Trial of Nebulized CF Candidate Therapy Completes Single-ascending Dosing
The RESTORE-CF clinical trial investigating Translate Bio’s candidate therapy MRT5005 has completed the single-ascending dose regimen in...


Specific Peptide May Lower Antibiotic Resistance of P. aeruginosa Bacteria, Study Reports
Expression of a peptide called RpoN* in antibiotic-resistant Pseudomonas aeruginosa isolates from cystic fibrosis (CF) patients made the...


Life-saving designer ‘NINJA virus’ hailed as medical breakthrough in curing infection
A VIRUS cocktail designed to seek and destroy bacteria has cleared a 15-year-old lung transplant patient of an antibiotic-resistant...


Lovelace Biomedical Talks About Developing Novel Therapies for Cystic Fibrosis Month
May is Cystic Fibrosis (CF) month. Lovelace has been working in respiratory research for over 70 years, and has been using gene therapy...

