mutation | mecfa 3/3

MECFA Blog

Gene Mutations Linked to Other Lung Diseases May Contribute to Bronchiectasis, Study Suggests

Mutations in genes linked to other lung diseases, specifically cystic fibrosis and primary ciliary dyskinesia, may also contribute to...

Health Canada Approves Symdeko to Treat CF Patients 12 and Up with Certain Gene Mutations

People ages 12 and older with cystic fibrosis (CF) who live in Canada can now be treated with Vertex Pharmaceuticals’ Symdeko...

Eluforsen for cystic fibrosis

ProQR is developing an investigational product, eluforsen (QR-010) for people with cystic fibrosis (CF) that have the F508del mutation....

Vertex’s VX-659 Triple Combo To Be Tested in Phase 3 Trial in Patients with 2 Copies of F508del Muta

Vertex Pharmaceuticals is launching a new Phase 3 trial to assess the triple combination of VX-659 plus tezacaftor (VX-661) and Kalydeco...

Cystic fibrosis drug Orkambi 'approved for use among 6-11 year olds'

The pharmaceutical firm making cystic fibrosis drug Orkambi says it has received EU approval to treat children. Manufacturer Vertex says...

CF Foundation | 2017 NACFC Plenary 1: Matching Medicines With Mutations

CF Foundation | Nonsense or Stop CF Mutations, e g , G542X

Disease Duration, Flare-ups Affect Mental Health of Non-CF Bronchiectasis Patients, Study Finds

VERTEX’S CF BLOCKBUSTER TRIKAFTA EFFECTIVE IN KIDS 6 TO 11 YEARS OF AGE

A case for improved carrier screening

Vertex to Seek Expanded FDA Approval for Trikafta After Positive Child Safety Data

Vertex’s Kaftrio approved for use in Europe and made accessible on the NHS

Age May Affect Outcomes in Lung Transplant Recipients With Cystic Fibrosis

CFF Funding Will Further ContraFect’s Research Into Alternative for Antibiotics

The search for molecular glue in targeted disease control

Vest Therapy Lowers Risk of Hospitalization in Non-CF Bronchiectasis, Study Says

Harvard is working with Boston hospitals to test existing cystic fibrosis drug to help coronavirus p

The Heartbreaking Reality of Cystic Fibrosis Care in Iraq: A Mother's Plea for Help

MECFA supports CF patients in Tunisia

International disparities in diagnosis and treatment access for cystic fibrosis

Philip Hopewell Prize for Global Respiratory Health Research

South Africans take on big pharma for access to ‘miracle’ cystic fibrosis drug

MECFA launches campaign to help people with CF in Gaza and the West Bank, Palestine

Ministry of Health unveils national electronic registry for cystic fibrosis patients

MECFA Jordan Project report

Conquering chronic lung infection in cystic fibrosis patients

Bacteria diversity in airways increases during babies’ first year