Vertex and Republic of Ireland Reach Agreement on Reimbursement for Triple Combination Therapy
Patients with cystic fibrosis (CF) in the Republic of Ireland will be among the first in Europe to benefit from Vertex Pharmaceuticals’...
5 New Drug Approvals the FDA Gave Top Priority
The U.S. Food and Drug Administration's made it clear that granting a priority review to an application isn't exactly the same thing as...
Long-awaited cystic fibrosis drug could turn deadly disease into a manageable condition
A new cystic fibrosis therapy dramatically improved patients’ lung function and showed clear signs of targeting the genetic root of the...
New Vertex cystic fibrosis drug approved, extending treatments to 90% of patients
Vertex Pharmaceuticals on Monday won approval for its fourth treatment for cystic fibrosis, a combination drug that extends a new form of...
5,000 Expected to Attend Cystic Fibrosis Conference, NACFC 2019, in Nashville
The Western Hemisphere’s largest gathering of experts in cystic fibrosis gets underway later this month in Nashville, Tennessee — site of...
Kalydeco’s Efficacy Tied to Phosphorylation Levels of CFTR Protein, Study Suggests
CFTR channel activity is controlled by a molecular process known as phosphorylation. Now, a study suggests that the levels of...